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Innovate
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International innovative drugs
Pombiliti
Pombiliti
departments:
内科
drug:
注射液
Active:
Cipaglucosidase alfa
indication:
Pombiliti用于治疗成人晚发性庞贝病(酸性α-葡萄糖苷酶[GAA]缺乏症)。Pombiliti与另一种药物miglustat联合使用。
Licensor:
Amicus Therapeutics Europe Limited
Approved Country/Region:
EMA
Approval time:
2023-03-20